4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
21 companies found
8 approved / 26 designated
16 designated · 0 approved
5 approved / 14 designated
4 approved / 10 designated
10 designated · 0 approved
5 designated · 0 approved
1 approved / 5 designated
1 approved / 4 designated
1 approved / 4 designated
4 designated · 0 approved
3 designated · 0 approved
3 designated · 0 approved
2 approved / 3 designated
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved