4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
26 companies found
70 approved / 109 designated
47 approved / 88 designated
34 approved / 57 designated
43 designated · 0 approved
41 designated · 0 approved
1 approved / 25 designated
19 designated · 0 approved
16 designated · 0 approved
11 approved / 15 designated
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved