4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
40 companies found
70 approved / 109 designated
34 approved / 57 designated
38 approved / 34 designated
15 designated · 0 approved
14 designated · 0 approved
9 designated · 0 approved
5 designated · 0 approved
5 designated · 0 approved
2 approved / 5 designated
5 designated · 0 approved
5 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
4 designated · 0 approved
3 designated · 0 approved
4 approved / 3 designated
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved