4170 companies with orphan drug designations or FDA approvals for this disease.
Orphan designations & approved drugs from FDA
Sponsor names unified across data sources
Companies linked to rare diseases & news
20 companies found
70 approved / 109 designated
23 approved / 67 designated
17 designated · 0 approved
14 designated · 0 approved
8 designated · 0 approved
2 approved / 5 designated
5 designated · 0 approved
1 approved / 4 designated
3 designated · 0 approved
3 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
2 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved
1 designated · 0 approved